The FDA has approved a new drug to treat a rare form of amyotrophic lateral sclerosis, or ALS. The drug is expected to help people with a very specific mutation, SOD1, which applies to about 2% of the ALS population.
Signage is seen outside of the Food and Drug Administration headquarters in White Oak, Maryland, on Aug. 29, 2020a new drug Tuesday to treat a rare form of amyotrophic lateral sclerosis, or ALS.
Studies showed that the drug reduced plasma neurofilament light , a blood-based biomarker of axonal injury and neurodegeneration, according to the FDA. Researchers determined Qalsody to be safe with the most common side effects being pain, fatigue, joint and muscle pain and increased white blood cells in cerebrospinal fluid.
The disease often begins with patients experiencing muscle twitching and weakness in one arm or leg followed by having difficulty swallowing or slurring speech.
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